I was looking at the list of drugs approved by FDA in 2014. I wanted to learn from successful cases. Most of the approved drugs were sponsored by big pharmas, but many of the drugs for rare diseases were sponsored by small biotechs. If we want to bring a new innovative drug to our patients with Wolfram syndrome, one of the solutions would be to create a small biotech focusing on Wolfram syndrome.
I hope you have a wonderful day. I have a lot to do and think.
Take care,
Fumi Urano