AAV for gene therapy?

What is AAV? AAV stands for adeno-associated virus. We have started using this type of virus. Why? Interestingly, AAV infects humans, but does not cause any disease. So doctors have started using this virus for gene therapy. We can create AAV expressing a gene of our interest, including MANF and WFS1. My idea is to use AAV expressing WFS1 and MANF for gene therapy.

Thank you for reading this blog. I am hopeful.

Take care,

Fumi Urano

Image: Dr Graham Beards at en.wikipedia [CC BY-SA 3.0 (http://creativecommons.org/licenses/by-sa/3.0) or GFDL (http://www.gnu.org/copyleft/fdl.html)], from Wikimedia Commons