Developing treatments for rare diseases: get the word out

Stephanie Snow Gebel, her daughter Raquel who has Wolfram syndrome, and myself were on ABC 30 News on Thursday. I received a large number of emails and phone calls yesterday. It seems like that the video is spreading through the internet right now. So I have started getting emails from all over the world. We were fortunate that Dr. Francis Collins, NIH Director, provided nice comments on the development of treatments for rare diseases. You can watch the video here.

Thank you so much for your encouragement. Raise Awareness, Improve Clinical Care, and Provide a Cure.

With confidence,

Fumi Urano