I attended the regenerative therapy group meeting on Friday and learned about the stem cell-based therapy for ALS, an incurable neurodegenerative disease. Clinical trials using this therapy are ongoing and at the Phase 2 stage.
Our regulatory system is designed to test drugs for common diseases, not for rare diseases. We should think about this together. I recommend you watch the TedTalk by physician-scientists, Jonathan Glass, MD and Nick Boulis, MD, who are developing and testing stem cell-based therapies for ALS.
http://www.tedmed.com/talks/show?id=7307
Thank you for your continued support.
Take care,
Fumi Urano