I have been testing the possibility that existing drugs for other disorders may be beneficial for Wolfram syndrome patients. This is called “drug repurposing.” This is not an crazy idea. For example, avastin which is licensed to treat various cancers is beneficial for patients with age-related macular degeneration (AMD) and diabetic retinopathy. Until we develop a drug specifically designed for Wolfram syndrome, I will keep on testing existing drugs.
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