As I mentioned in my yesterday’s blog, I have three things always on my mind, and one of them is to develop novel treatment for Wolfram syndrome. I would like to develop three different types of treatment, drugs, biologics, and stem cell-based therapy combined with DNA editing. To identify and develop drugs, we need drug screening systems. We have been trying to develop multiple systems. We have just published one of our systems. We can use this “cell-based assay” to identify new drugs for Wolfram and diabetes.
http://press.endocrine.org/doi/pdf/10.1210/me.2014-1260
I am hopeful and grateful. I feel that something wonderful is going to happen to us today.
Warmly,
Fumi Urano